Gene and Stem Cell Therapies

P11: From Well to Bed: Stem Cell Therapies for Neurotrauma

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Gene and Stem Cell Therapies for Treating Epilepsy

Introduction .................................................................................................................................... 583 Background .................................................................................................................................... 584 Gene Therapy for Temporal Lobe Epilepsy ..............................................................

Gene, Stem Cell, and Alternative Therapies for SCA 1

Spinocerebellar ataxia 1 is an autosomal dominant disease characterized by neurodegeneration and motor dysfunction. In disease pathogenesis, polyglutamine expansion within Ataxin-1, a gene involved in transcriptional repression, causes protein nuclear inclusions to form. Most notably, neuronal dysfunction presents in Purkinje cells. However, the effect of mutant Ataxin-1 is not entirely underst...

Gene, stem cell, and future therapies for orphan diseases.

There are an estimated 7,000 "orphan diseases," but treatments are currently available for only about 5% of them. Recent progress in the advanced platforms of gene therapy, stem cell therapy, gene modification, and gene correction offers possibilities for new therapies and cures for rare diseases. Many rare diseases are genetic in origin, and gene therapy is being successfully applied to treat ...

Advances in Stem Cell Therapies